Neurogene Inc.’s NGNE share price has dipped by 18.34%, which has investors questioning if this is right time to buy.

The family of nine-year-old Charleigh Pollock will continue to be covered for the drug, which costs $1 million a year, until ...

A temporary reprieve for a Vancouver Island family after their terminally-ill daughter will continue to have access to ...

The father of a nine-year-old girl with a rare disease likened to childhood dementia has called for health bosses to prolong access to a "miraculous" treatment. Addy Clarke, from Swindon, was four ...

A charity walk is to be held to raise funds to help support a Doncaster youngster battling a terminal genetic disease.Five ...

Her son, Isaac, eight, had CLN2 Batten disease diagnosed in August 2021. It is an incurable condition which causes childhood dementia, epilepsy and loss of sight. Ms Tilley said: "It is agonising.

The mother of a six-year-old girl with a rare neurodegenerative disease has urged health bosses to "do the right thing" amid fears over the future of the medication she takes. Flory, from Coventry, ...

Funding for Charleigh's life-sustaining medication has been extended for another three months, according to her mom.

Provincial funding of 9-year-old Charleigh Pollock's life-sustaining treatment has been extended by 3 months until the end of ...

Nine-year-old Charleigh Pollock has a neurological disorder called Batten disease that leaves her with recurring severe seizures and mobility loss, and will eventually cut her young life short.