PTC Therapeutics, Inc. (NASDAQ: PTCT) today shared new data being presented from the Phase 3 APHENITY trial and subsequent open-label extension study at the 2025 American College of Medical Genetics ...

PTC Therapeutics (PTCT) shared new data being presented from the Phase 3 APHENITY trial and subsequent open-label extension study at the 2025 ...

BioMarin (BMRN) announced positive new data from studies of Voxzogo in children with achondroplasia and in ongoing clinical trials ...

Phenylketonuria (PKU) is a disorder where an amino acid called phenylalanine accumulates inappropriately in the body. Phenylalanine is a protein building block the body obtains through the ...

A new study suggests early detection improves outcomes, but metabolic episodes in the first days of life still prove ...

Atlanta-based workers are baffled by Trump administration cuts to research that directly supports departmental health improvement goals.

Given the chatter that this is a gold-standard ingredient for hair growth, you may be super tempted to hit "add to cart" on ...

Synlogic (NASDAQ:SYBX – Get Free Report) is expected to issue its quarterly earnings data on Tuesday, March 18th. Analysts ...

For example, a common treatment option for patients with phenylketonuria, which causes an increase in phenylalanine levels, is an avoidance of high-protein foods. Phenylketonuria affects one in 25,000 ...

A nutritionist has warned people to avoid constantly using sweeteners over sugar as she claims the former is 'worse' and can ...

A nutritionist has warned of the dangers of consuming too many sweeteners instead of sugar. Everyday household sugar, often ...

Personal health and wellness is one of the many secular tailwinds for healthcare companies. Despite the rosy long-term ...