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Washington DC - Almost six years ago, Fatiha and Abellatif Abderraziq stood in the parking lot of Washington children’s ...
Newborn screening offers every child a safer, healthier start by enabling early detection, timely care, and improved outcomes ...
Given their life-saving potential, newborn screenings should not be seen as optional but as a fundamental part of postnatal ...
SAN RAFAEL, CA, USA I April 2, 2025 I BioMarin Pharmaceutical Inc. (Nasdaq: BMRN) today announced that the Phase 3 PEGASUS trial evaluating PALYNZIQ ® (pegvaliase-pqpz) met its primary efficacy ...
U.S. newborn screening programs began in the early 1960s with phenylketonuria (PKU), a disorder of protein metabolism that causes mental retardation when untreated. Babies with PKU appear normal ...
Global Newborn Screening Market is projected to grow at a CAGR of ~6–8% from 2022 to 2027. This is likely to be driven by an ...
BioMarin BMRN has announced positive results from the phase III PEGASUS study evaluating Palynziq (pegvaliase) in adolescents aged 12-17 years with phenylketonuria (PKU). The study achieved its ...
Nursing influencer Hailey Okula’s husband, Matthew Okula, is trying his best to turn his pain into purpose. Earlier this week ...