After getting a green light from the European Commission, Biogen’s Skyclarys is the first approved medicine for the inherited neurological disease Friedreich’s ataxia (FA) in the EU.

He also served as CMO at Fate Therapeutics, where he filed the first investigational new ... starting with DT-216P2 for Friedreich ataxia. I look forward to applying my experience to further ...

The apparent end of large-scale U.S. foreign aid is a crisis that also creates an opportunity. Trump’s “America First” policies are now reality for the next four years, if not longer.

CARLSBAD, Calif., April 21, 2025 (GLOBE NEWSWIRE) -- Design Therapeutics, Inc. (Nasdaq: DSGN), a clinical-stage biotechnology company developing treatments for serious degenerative genetic ...

As of Spring 2025, Sling Orange is $46 per month and Sling Blue costs $51. (You’ll get a discount on your first month.) Or if you get Sling Orange and Sling Blue, it’ll cost $66 a month.

On 1 October 2013, the Health and Safety (First Aid) Regulations 1981 (the Regulations ... sprains and strains and rarely head and spinal injuries. Early Years staff should also have a first aider. In ...

This important study investigates the molecular mechanisms by which the p53 isoforms Δ133p53α and Δ160p53α exert dominant-negative effects on full-length p53 (FLp53). Through a combination of ...

But there's also the more positive news that Ukraine and the US have taken the first steps towards striking a long-awaited minerals deal - something we told you about earlier in our 8.40am post.

The injuries were either confined to the musculoskeletal structures with or without spinal cord involvement. The fracture dislocations presented with thoraco-lumbar deformity, kyphosis or ...

connective tissue of tendons and joints or central nervous system including brain with or without spinal cord anomalies.2 A total of 402 genes have been reported so far in AMC.3 There are multiple ...