Vertex Pharmaceuticals (Nasdaq: VRTX) today announced that the European Commission has granted regulatory approval for a ...

Hirschsprung disease and meconium ileus can both cause a newborn to be unable to pass their first stool. Learn the different ...

Discover how an emerging technology called tRNA therapy could become the next big thing in genetic disease treatment.

Cystic Fibrosis Ireland sees an increasingly complex picture of what it means to be an older person living with CF ...

Survivor star Luke Toki has opened about his six-year-old daughter Maddie's recent health battle. The 38-year-old reality ...