The mother of a six-year-old girl with a rare neurodegenerative disease has urged health bosses to "do the right thing" amid ...

A mother has spoken about her "painful" experience over the potential end to her son's life-enhancing treatment for a rare ...

Jessica Rich, nine, has a very rare and serious illness called Batten disease, but her life-saving drug could be about to be ...

Siblings Ollie, 14, and Amelia Carroll, 12, both have Batten Disease, which is an incurable genetic disorder that causes rapid decline in a child's ability to walk, talk and see. Even though the ...

CLN2 Batten disease is an incurable genetic disorder that causes rapid decline in a child's ability to walk, talk and see. Phoebe, from Coventry, said daughter Flory's doses of Brineura ...

Two years ago, Beatrice Cieslik was diagnosed with CLN2 type Batten disease - a rare degenerative condition which causes seizures, blindness, dementia, and difficulty with mobility and speech.

A life-saving medicine for children with Batten disease, a rare and fatal genetic disorder, is set to be pulled from the ...

NGNE to update on a potential registrational phase 3 study, using NGN-401, for the treatment of patients with Rett Syndrome.

Two years ago, Beatrice Cieslik was diagnosed with CLN2 type Batten disease - a rare degenerative condition which causes seizures, blindness, dementia, and difficulty with mobility and speech. She is ...

James Forrest Skaggs, age 79, of Greenfield, passed away on Wednesday, February 19, 2025 at Ascension St. Vincent Hospital. He was born in Indianapolis on May 27, 1945 to Forrest and Myrtle ...